One-Time gene injection aims to tame devastating childhood seizures
Disease control
Recruiting now
This study is testing a one-time gene therapy called ETX101 for children with Dravet syndrome, a severe form of epilepsy. The goal is to see if delivering a corrected gene directly to the brain can safely reduce the number of seizures and improve a child's learning and developmen…
Phase: PHASE1, PHASE2 • Sponsor: Encoded Therapeutics • Aim: Disease control
Last updated Apr 02, 2026 07:27 UTC