Gene therapy trial aims to tame severe seizures in kids with dravet syndrome
Disease control
Recruiting now
This study tests a gene therapy called ETX101 in infants and children with Dravet syndrome, a severe genetic epilepsy. The treatment delivers a working gene to help control seizures and improve development. The study involves about 47 participants across different age groups and …
Phase: PHASE1, PHASE2 • Sponsor: Encoded Therapeutics • Aim: Disease control
Last updated May 26, 2026 13:29 UTC