MYOTONIC DYSTROPHY TYPE 1 (DM1)
Clinical trials for MYOTONIC DYSTROPHY TYPE 1 (DM1) explained in plain language.
Never miss a new study
Get alerted when new MYOTONIC DYSTROPHY TYPE 1 (DM1) trials appear
Sign up with your email to follow new studies for MYOTONIC DYSTROPHY TYPE 1 (DM1), keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
Genom att skicka in godkänner du våra Användarvillkor
-
New drug DYNE-101 aims to ease muscle stiffness in rare disease
Disease control Recruiting nowThis study tests a new drug, DYNE-101, in 116 adults with myotonic dystrophy type 1 (DM1), a condition that causes muscle weakness and stiffness. The main goal is to see if the drug is safe and tolerable, and to measure its effects on muscle function and disease markers. Particip…
Matched conditions: MYOTONIC DYSTROPHY TYPE 1 (DM1)
Phase: PHASE1, PHASE2 • Sponsor: Dyne Therapeutics • Aim: Disease control
Last updated May 26, 2026 07:11 UTC
-
New hope for DM1: vertex launches First-in-Human trial of VX-670
Disease control Recruiting nowThis early-stage trial tests the safety and tolerability of a new drug called VX-670 in 44 adults with myotonic dystrophy type 1 (DM1), a genetic condition that causes muscle weakness and other problems. Participants receive either single or multiple doses of VX-670 or a placebo.…
Matched conditions: MYOTONIC DYSTROPHY TYPE 1 (DM1)
Phase: PHASE1, PHASE2 • Sponsor: Vertex Pharmaceuticals Incorporated • Aim: Disease control
Last updated May 26, 2026 07:04 UTC
-
New drug trial hopes to ease muscle stiffness in rare disease
Disease control Recruiting nowThis study tests a new medicine, DYNE-101, for adults with myotonic dystrophy type 1, a condition that causes muscle weakness and stiffness. About 150 people will receive either the drug or a placebo for 48 weeks. The goal is to see if the drug improves muscle function, like stan…
Matched conditions: MYOTONIC DYSTROPHY TYPE 1 (DM1)
Phase: PHASE3 • Sponsor: Dyne Therapeutics • Aim: Disease control
Last updated May 20, 2026 11:57 UTC
-
Music sessions tested as therapy for rare muscle disease
Symptom relief Recruiting nowThis study explores whether weekly music and movement classes are practical and enjoyable for children aged 6–18 with myotonic dystrophy type 1 (DM1). Over 10 weeks, 13 participants will attend 45-minute sessions, wear activity trackers, and provide biological samples. The goal i…
Matched conditions: MYOTONIC DYSTROPHY TYPE 1 (DM1)
Phase: NA • Sponsor: Hanns Lochmuller • Aim: Symptom relief
Last updated May 26, 2026 06:52 UTC
-
No travel needed: new study aims to unravel mysteries of myotonic dystrophy
Knowledge-focused Recruiting nowThis study looks at why myotonic dystrophy type 1 affects people so differently—some have mild symptoms, others severe. Researchers will measure muscle strength, memory, and activity using tools mailed to your home, and analyze your DNA from a blood sample. The goal is to better …
Matched conditions: MYOTONIC DYSTROPHY TYPE 1 (DM1)
Sponsor: University of Rochester • Aim: Knowledge-focused
Last updated May 26, 2026 07:07 UTC