Myotonic dystrophy type 1 (DM1)
Clinical trials for Myotonic dystrophy type 1 (DM1) explained in plain language.
Never miss a new study
Get alerted when new Myotonic dystrophy type 1 (DM1) trials appear
Sign up with your email to follow new studies for Myotonic dystrophy type 1 (DM1), keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
Genom att skicka in godkänner du våra Användarvillkor
-
New hope for muscle disease: experimental drug VX-670 enters human trials
Disease control OngoingThis early-stage trial tests the safety and tolerability of a new drug called VX-670 in 52 adults with myotonic dystrophy type 1 (DM1), a genetic condition that causes muscle weakness and other problems. Participants receive either VX-670 or a placebo, and researchers will monito…
Matched conditions: MYOTONIC DYSTROPHY TYPE 1 (DM1)
Phase 1/2 • Sponsor: Vertex Pharmaceuticals Incorporated • Aim: Disease control
Last updated Aug 22, 2026 00:00 UTC
-
Vertex tests long-term safety of VX-670 for muscle disease
Disease control By invitation onlyThis study tests the long-term safety and effectiveness of an experimental drug called VX-670 in adults with myotonic dystrophy type 1 (DM1). Participants who completed a previous VX-670 study can join. The drug is given through a vein, and researchers will monitor side effects a…
Matched conditions: MYOTONIC DYSTROPHY TYPE 1 (DM1)
Phase 2 • Sponsor: Vertex Pharmaceuticals Incorporated • Aim: Disease control
Last updated Aug 12, 2026 00:00 UTC
-
Music therapy tested for rare muscle disease in kids
Symptom relief OngoingThis study explores whether weekly music and movement sessions are practical and enjoyable for children aged 6 to 18 with myotonic dystrophy type 1 (DM1). Over 10 weeks, participants attend 45-minute music classes, undergo physical and cognitive tests, and provide biological samp…
Matched conditions: MYOTONIC DYSTROPHY TYPE 1 (DM1)
Sponsor: Hanns Lochmuller • Aim: Symptom relief
Last updated Jul 30, 2026 00:00 UTC