MYOTONIC DYSTROPHY TYPE 1 (DM1)
Clinical trials for MYOTONIC DYSTROPHY TYPE 1 (DM1) explained in plain language.
Never miss a new study
Get alerted when new MYOTONIC DYSTROPHY TYPE 1 (DM1) trials appear
Sign up with your email to follow new studies for MYOTONIC DYSTROPHY TYPE 1 (DM1), keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
Genom att skicka in godkänner du våra Användarvillkor
-
New drug trial targets debilitating muscle disease
Disease control Recruiting nowThis study is testing an investigational drug called DYNE-101 for adults with myotonic dystrophy type 1 (DM1), a genetic disorder that causes progressive muscle weakness and stiffness. The main goals are to see if the drug is safe and if it can improve muscle function and reduce …
Matched conditions: MYOTONIC DYSTROPHY TYPE 1 (DM1)
Phase: PHASE1, PHASE2 • Sponsor: Dyne Therapeutics • Aim: Disease control
Last updated Apr 01, 2026 14:43 UTC
-
New drug trial offers hope for genetic muscle disease
Disease control Recruiting nowThis early-stage study is testing a new drug called VX-670 in adults with myotonic dystrophy type 1, a genetic muscle-wasting disease. Researchers will give different doses to 44 participants to check if the drug is safe and how it behaves in the body. The study will also measure…
Matched conditions: MYOTONIC DYSTROPHY TYPE 1 (DM1)
Phase: PHASE1, PHASE2 • Sponsor: Vertex Pharmaceuticals Incorporated • Aim: Disease control
Last updated Mar 19, 2026 14:55 UTC
-
Can music and movement ease symptoms of a rare muscle disease in kids?
Symptom relief Recruiting nowThis study is testing whether weekly music and movement sessions are practical and helpful for children with congenital myotonic dystrophy type 1 (DM1), a rare genetic disorder that affects muscles, the brain, and the heart. Researchers will see if these sessions can improve phys…
Matched conditions: MYOTONIC DYSTROPHY TYPE 1 (DM1)
Phase: NA • Sponsor: Hanns Lochmuller • Aim: Symptom relief
Last updated Mar 31, 2026 12:11 UTC
-
Scientists launch major At-Home study to unlock mysteries of variable muscle disease
Knowledge-focused Recruiting nowThis study aims to better understand why symptoms of myotonic dystrophy type 1 (DM1) vary so much between people. Researchers will work remotely with 1,000 adults who have DM1 to measure symptoms like strength and memory and analyze their genetics from a blood sample. The goal is…
Matched conditions: MYOTONIC DYSTROPHY TYPE 1 (DM1)
Sponsor: University of Rochester • Aim: Knowledge-focused
Last updated Apr 03, 2026 14:41 UTC