AUTOSOMAL RECESSIVE HYPOPHOSPHATEMIC RICKETS
Clinical trials for AUTOSOMAL RECESSIVE HYPOPHOSPHATEMIC RICKETS explained in plain language.
Never miss a new study
Get alerted when new AUTOSOMAL RECESSIVE HYPOPHOSPHATEMIC RICKETS trials appear
Sign up with your email to follow new studies for AUTOSOMAL RECESSIVE HYPOPHOSPHATEMIC RICKETS, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
Genom att skicka in godkänner du våra Användarvillkor
-
First treatment tested for babies with deadly artery hardening disease
Disease control Recruiting nowThis study is testing a new enzyme replacement therapy called INZ-701 in infants with rare genetic disorders that cause dangerous calcium buildup in arteries and weak bones. The main goal is to check if the treatment is safe and well-tolerated in babies under one year old. Resear…
Matched conditions: AUTOSOMAL RECESSIVE HYPOPHOSPHATEMIC RICKETS
Phase: PHASE1 • Sponsor: Inozyme Pharma • Aim: Disease control
Last updated Apr 01, 2026 14:42 UTC
-
Hope for babies with Ultra-Rare fatal disease: experimental drug enters final testing phase
Disease control Recruiting nowThis study is testing an investigational drug called INZ-701 in infants with a severe, ultra-rare genetic disorder called ENPP1 deficiency. The main goals are to see if the drug improves survival and prevents dangerous calcium buildup in the heart and blood vessels. About 12 infa…
Matched conditions: AUTOSOMAL RECESSIVE HYPOPHOSPHATEMIC RICKETS
Phase: PHASE3 • Sponsor: Inozyme Pharma • Aim: Disease control
Last updated Mar 23, 2026 15:16 UTC