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New hope for babies with rare calcification diseases: drug trial launches

NCT ID NCT05734196

First seen Mar 29, 2026 · Last updated May 22, 2026 · Updated 8 times

Summary

This early-stage study tests a new medicine called INZ-701 in up to 16 infants (up to 1 year old) who have rare genetic conditions that cause dangerous calcium buildup in blood vessels and bones. The main goal is to check if the drug is safe and how it affects the body, especially the heart. Researchers will also measure changes in blood markers and look for any side effects.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Boston Children's Hospital

    WITHDRAWN

    Boston, Massachusetts, 02115, United States

  • Hospital Sant Joan de Déu

    TERMINATED

    Barcelona, Spain

  • Nationwide Children's Hospital

    RECRUITING

    Columbus, Ohio, 43205, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Rady Children's Hospital

    RECRUITING

    San Diego, California, 92123, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Royal Manchester Children's Hospital

    TERMINATED

    Manchester, M13 9WL, United Kingdom

  • The Children's Hospital of Philadelphia

    RECRUITING

    Philadelphia, Pennsylvania, 19104, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • The University of Utah

    WITHDRAWN

    Salt Lake City, Utah, 84108, United States

Conditions

Explore the condition pages connected to this study.