New hope for babies with rare calcification disease: experimental drug enters human testing
NCT ID NCT05734196
First seen Mar 29, 2026 · Last updated May 14, 2026 · Updated 7 times
Summary
This study tests an experimental drug called INZ-701 in 16 infants (up to 1 year old) with rare genetic conditions (ENPP1 or ABCC6 deficiency) that cause dangerous calcium buildup in blood vessels and other tissues. The main goal is to check the drug's safety and how the body processes it. Researchers will monitor side effects, heart function, and blood markers to see if the drug can help control the disease.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Boston Children's Hospital
WITHDRAWNBoston, Massachusetts, 02115, United States
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Hospital Sant Joan de Déu
TERMINATEDBarcelona, Spain
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Nationwide Children's Hospital
RECRUITINGColumbus, Ohio, 43205, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Rady Children's Hospital
RECRUITINGSan Diego, California, 92123, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Royal Manchester Children's Hospital
TERMINATEDManchester, M13 9WL, United Kingdom
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The Children's Hospital of Philadelphia
RECRUITINGPhiladelphia, Pennsylvania, 19104, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact Phone: •••-•••-•••• Email: •••••@•••••
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The University of Utah
WITHDRAWNSalt Lake City, Utah, 84108, United States
Conditions
Explore the condition pages connected to this study.