AUTOSOMAL RECESSIVE HYPOPHOSPHATEMIC RICKETS
Clinical trials for AUTOSOMAL RECESSIVE HYPOPHOSPHATEMIC RICKETS explained in plain language.
Never miss a new study
Get alerted when new AUTOSOMAL RECESSIVE HYPOPHOSPHATEMIC RICKETS trials appear
Sign up with your email to follow new studies for AUTOSOMAL RECESSIVE HYPOPHOSPHATEMIC RICKETS, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
By submitting, you agree to our Terms of use
-
New hope for babies with rare calcification disease: first drug trial launches
Disease control Recruiting nowThis study tests a new drug called INZ-701 in up to 16 infants (up to 1 year old) with rare genetic conditions (ENPP1 or ABCC6 deficiency) that cause dangerous calcium buildup in arteries and other problems. The main goal is to check the drug's safety and how the body handles it,…
Matched conditions: AUTOSOMAL RECESSIVE HYPOPHOSPHATEMIC RICKETS
Phase: PHASE1 • Sponsor: Inozyme Pharma • Aim: Disease control
Last updated Jun 27, 2026 12:00 UTC
-
New hope for babies: drug targets rare genetic disorder that hardens arteries
Disease control Recruiting nowThis study tests a new medicine called INZ-701 in babies up to 1 year old who have a rare genetic condition (ENPP1 deficiency) that causes severe hardening of the arteries and bone problems. The goal is to see if the drug can raise a key substance in the blood, improve survival, …
Matched conditions: AUTOSOMAL RECESSIVE HYPOPHOSPHATEMIC RICKETS
Phase: PHASE3 • Sponsor: Inozyme Pharma • Aim: Disease control
Last updated Jun 27, 2026 11:03 UTC