ATP-BINDING CASSETTE SUBFAMILY C MEMBER 6 DEFICIENCY
Clinical trials for ATP-BINDING CASSETTE SUBFAMILY C MEMBER 6 DEFICIENCY explained in plain language.
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New hope for babies with rare calcification diseases: drug trial launches
Disease control Recruiting nowThis early-stage study tests a new medicine called INZ-701 in up to 16 infants (up to 1 year old) who have rare genetic conditions that cause dangerous calcium buildup in blood vessels and bones. The main goal is to check if the drug is safe and how it affects the body, especiall…
Matched conditions: ATP-BINDING CASSETTE SUBFAMILY C MEMBER 6 DEFICIENCY
Phase: PHASE1 • Sponsor: Inozyme Pharma • Aim: Disease control
Last updated May 26, 2026 09:04 UTC
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New registry aims to unlock secrets of rare genetic diseases
Knowledge-focused Recruiting nowThis study is a registry that collects information from people with two rare genetic conditions: ENPP1 deficiency and infantile-onset ABCC6 deficiency. Researchers will gather data from routine doctor visits and patient questionnaires to understand how these diseases progress and…
Matched conditions: ATP-BINDING CASSETTE SUBFAMILY C MEMBER 6 DEFICIENCY
Sponsor: Inozyme Pharma • Aim: Knowledge-focused
Last updated May 26, 2026 08:59 UTC