New drug YA-101 aims to slow rare brain disease

NCT ID NCT06848231

First seen Jun 24, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This Phase 2 trial tests the safety and effectiveness of YA-101, an oral drug, in 75 people with multiple system atrophy (MSA), a rare and progressive brain disorder. Participants will receive either YA-101 or a placebo twice daily for several weeks. The study will monitor side effects and measure drug levels in the blood to see if YA-101 can help control the disease.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

YA-101

What this could lead to

If it works, this could point toward a treatment that slows or controls multiple system atrophy, a rare and devastating brain disease.

What could go wrong

This is an early Phase 2 trial with only 75 participants, so results may not apply to everyone. The drug may not work or could cause side effects.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

multiple system atrophy

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Baylor College of Medicine

    RECRUITING

    Houston, Texas, 77030, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Brigham and Women's Hospital

    RECRUITING

    Boston, Massachusetts, 02115, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Columbia University Irving medical center

    RECRUITING

    New York, New York, 10032, United States

    Contact Phone: •••-•••-••••

  • Juntendo University Hospital

    RECRUITING

    Tokyo, Japan

  • Mayo Clinic

    RECRUITING

    Rochester, Minnesota, 55905, United States

  • National Taiwan University Hospital

    RECRUITING

    Taipei, 100225, Taiwan

    Contact Email: •••••@•••••

  • National Taiwan University Hospital Cancer Center

    NOT_YET_RECRUITING

    Taipei, 106, Taiwan

  • UCLA Health

    RECRUITING

    Los Angeles, California, 90095, United States

    Contact Phone: •••-•••-••••

  • Vanderbilt University Medical Center

    RECRUITING

    Nashville, Tennessee, 37232, United States

    Contact Email: •••••@•••••