New hope for kids with rare immune disease: trametinib trial launched

NCT ID NCT04943224

First seen Mar 28, 2026 · Last updated May 22, 2026 · Updated 9 times

Summary

This study looks at how to best use the drug trametinib in children with histiocytosis, a rare disease where immune cells build up and cause damage. It is for kids whose disease did not respond to standard treatments or who do not have the BRAF gene change. The goal is to find the right dose and timing to control the disease and prevent it from coming back.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Mother and Child Institute

    RECRUITING

    Warsaw, Mazovian, 01-211, Poland

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.