Milder stem cell transplant offers hope for Non-Cancer blood disorders
NCT ID NCT00920972
First seen Feb 28, 2026 · Last updated Apr 30, 2026 · Updated 14 times
Summary
This study tests a less intense stem cell transplant for people with non-cancerous blood, immune, or metabolic disorders. The goal is to see if a milder preparation helps donor cells take hold safely. About 220 participants will be enrolled to monitor engraftment and side effects within the first 100 days.
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This is a summary of
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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All Children's Hospital
COMPLETEDSt. Petersburg, Florida, 33701, United States
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BC Children's Hospital
COMPLETEDVancouver, British Columbia, V6H 3N1, Canada
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Carolinas Medical Center
COMPLETEDCharlotte, North Carolina, 28232, United States
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Children's Hospital of New Orleans
COMPLETEDNew Orleans, Louisiana, 70118, United States
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Children's Hospital of Orange County
RECRUITINGOrange, California, 92868, United States
Contact
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Children's Memorial Hospital
COMPLETEDChicago, Illinois, 60614, United States
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Children's Mercy
COMPLETEDKansas City, Missouri, 64108, United States
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Columbia University Medical Center
RECRUITINGNew York, New York, 10032, United States
Contact
Contact
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Cook Children's Hospital
COMPLETEDForth Worth, Texas, 76104, United States
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Duke Children's Hospital
COMPLETEDDurham, North Carolina, 27705, United States
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George Washington University School of Medicine
RECRUITINGWashington D.C., District of Columbia, 20010, United States
Contact
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Hackensack University Medical Center
COMPLETEDHackensack, New Jersey, 07601, United States
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Indiana University School of Medicine
RECRUITINGIndianapolis, Indiana, 46202, United States
Contact
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Miami Children's Hospital
COMPLETEDMiami, Florida, 33155, United States
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Nemours Children's Health
COMPLETEDJacksonville, Florida, 32207, United States
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Phoenix Children's Hospital
RECRUITINGPhoenix, Arizona, 85016, United States
Contact
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St. Louis University
RECRUITINGSt Louis, Missouri, 63104, United States
Contact
Contact
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Texas Transplant Institute
COMPLETEDSan Antonio, Texas, 78229, United States
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The University of Oklahoma
COMPLETEDOklahoma City, Oklahoma, 73104, United States
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University of Calgary
COMPLETEDCalgary, Canada
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University of California
RECRUITINGSan Diego, California, 92123, United States
Contact
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University of Manitoba
COMPLETEDWinnipeg, Manitoba, MB R3E 0T4, Canada
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University of Miami
RECRUITINGMiami, Florida, 33136, United States
Contact
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University of North Carolina
RECRUITINGChapel Hill, North Carolina, 27514, United States
Contact
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University of Pittsburg
COMPLETEDPittsburgh, Pennsylvania, 15224, United States
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University of Utah
RECRUITINGSalt Lake City, Utah, 84132, United States
Contact
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Washington University School of Medicine (in St. Louis)
RECRUITINGSt Louis, Missouri, 63110, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Yale School of Medicine
RECRUITINGNew Haven, Connecticut, 06510, United States
Contact
Conditions
Explore the condition pages connected to this study.