New transplant trial aims to reset immune system in rare genetic disorder
NCT ID NCT01861106
Summary
This study is testing whether a stem cell transplant from a donor can treat GATA2 deficiency, a genetic condition that causes serious infections and blood cancers. Participants (ages 6-70) will receive chemotherapy and then donor stem cells to try to rebuild their immune system. The goal is to see if the transplant can restore healthy blood cell production and reverse the disease's effects.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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National Institutes of Health Clinical Center
RECRUITINGBethesda, Maryland, 20892, United States
Conditions
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