Can a common drug slow vision loss in rare wolfram syndrome?

NCT ID NCT03717909

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This study tested a drug called sodium valproate in 63 children and adults with Wolfram syndrome, a rare genetic disorder that causes vision loss and other health problems. Participants were randomly assigned to receive either the drug or a placebo to see if it could slow the worsening of eyesight. The trial was stopped early in 2022, and the results will help determine if this treatment is safe and effective for managing the disease.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for WOLFRAM SYNDROME are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Conditions

The condition(s) this trial relates to.

Wolfram syndrome

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Birmingham Women's and Children's Hospital

    Birmingham, B4 6NH, United Kingdom

  • CHU de Montpellier, Hopital Gui de Chauliac

    Montpellier, 34295, France

  • Hôpital Européen Georges-Pompidou

    Paris, 75015, France

  • Medical University of Lodz

    Lodz, 91-738, Poland

  • Unidad de Gestión Clínica Almería Periferia. Distrito Sanitario Almería

    Almería, 04120, Spain

  • University Hospitals Birmingham

    Birmingham, B15 2TH, United Kingdom