Can a common drug slow vision loss in rare wolfram syndrome?
NCT ID NCT03717909
First seen Jun 27, 2026 · Last updated Jun 27, 2026
Summary
This study tested a drug called sodium valproate in 63 children and adults with Wolfram syndrome, a rare genetic disorder that causes vision loss and other health problems. Participants were randomly assigned to receive either the drug or a placebo to see if it could slow the worsening of eyesight. The trial was stopped early in 2022, and the results will help determine if this treatment is safe and effective for managing the disease.
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the original study
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
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Locations
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Birmingham Women's and Children's Hospital
Birmingham, B4 6NH, United Kingdom
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CHU de Montpellier, Hopital Gui de Chauliac
Montpellier, 34295, France
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Hôpital Européen Georges-Pompidou
Paris, 75015, France
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Medical University of Lodz
Lodz, 91-738, Poland
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Unidad de Gestión Clínica Almería Periferia. Distrito Sanitario Almería
Almería, 04120, Spain
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University Hospitals Birmingham
Birmingham, B15 2TH, United Kingdom