Drug trial aims to slow vision loss in rare wolfram syndrome
NCT ID NCT03717909
First seen May 06, 2026 · Last updated May 06, 2026
Summary
This study tested the drug sodium valproate in 63 children and adults with Wolfram syndrome, a rare genetic disorder that causes vision loss, diabetes, and other problems. Participants were randomly assigned to receive either the drug or a placebo. The main goal was to see if the drug could slow the worsening of eyesight. The trial was stopped early in 2022, and results are being analyzed to determine if the treatment is safe and effective.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Birmingham Women's and Children's Hospital
Birmingham, B4 6NH, United Kingdom
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CHU de Montpellier, Hopital Gui de Chauliac
Montpellier, 34295, France
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Hôpital Européen Georges-Pompidou
Paris, 75015, France
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Medical University of Lodz
Lodz, 91-738, Poland
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Unidad de Gestión Clínica Almería Periferia. Distrito Sanitario Almería
Almería, 04120, Spain
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University Hospitals Birmingham
Birmingham, B15 2TH, United Kingdom
Conditions
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