New drug trial aims to slow rare wolfram syndrome
NCT ID NCT05676034
First seen Apr 22, 2026 · Last updated May 14, 2026 · Updated 4 times
Summary
This study tests an experimental drug called AMX0035 in 12 adults with Wolfram syndrome, a rare genetic disorder that causes diabetes and vision loss. The goal is to see if the drug can protect insulin-producing cells and is safe over up to 4 years. Participants take the drug by mouth and wear a continuous glucose monitor.
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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Locations
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Washington University
St Louis, Missouri, 63110, United States
Conditions
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