New hope for brain tumor patients: targeted drug shows promise in phase 3 trial

NCT ID NCT05303519

First seen Jun 27, 2026 · Last updated Jul 02, 2026 · Updated 2 times

Summary

This study tests a drug called safusidenib in people with a type of brain tumor (glioma) that has a specific gene mutation (IDH1). The trial has three parts: one for recurrent tumors, one for high-risk tumors after standard treatment, and one for a specific tumor type after surgery alone. The goal is to see if the drug can control the tumor and improve survival.

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Conditions

The condition(s) this trial relates to.

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Beijing Tiantan Hospital, Capital Medical University

    RECRUITING

    Beijing, Beijing Municipality, 100070, China

  • Billings Clinic

    RECRUITING

    Billings, Montana, 59101, United States

  • Cleveland Clinic

    RECRUITING

    Cleveland, Ohio, 44106, United States

  • Columbia University Medical Center

    RECRUITING

    New York, New York, 10032, United States

    Contact Email: •••••@•••••

  • Dana-Farber Cancer Institute

    RECRUITING

    Boston, Massachusetts, 02215, United States

  • Duke Cancer Institute

    RECRUITING

    Durham, North Carolina, 27710, United States

  • Fred Hutch Cancer Center

    RECRUITING

    Seattle, Washington, 98195, United States

  • Henry Ford Hospital

    RECRUITING

    Detroit, Michigan, 48202, United States

  • Hoag Memorial Hospital Presbyterian

    RECRUITING

    Newport Beach, California, 92663, United States

  • Huashan Hospital Affiliated to Fudan University

    RECRUITING

    Shanghai, Shanghai Municipality, 200040, China

  • Huntsman Cancer Insititute, University of Utah

    RECRUITING

    Salt Lake City, Utah, 84112, United States

  • Icahn School of Medicine at Mount Sinai

    NOT_YET_RECRUITING

    New York, New York, 10029, United States

  • Indiana University

    RECRUITING

    Indianapolis, Indiana, 46202, United States

  • Inova Schar Cancer Institute

    NOT_YET_RECRUITING

    Fairfax, Virginia, 22031, United States

  • MD Anderson Cancer Center

    RECRUITING

    Houston, Texas, 77030, United States

  • Massachusetts General Hospital

    RECRUITING

    Boston, Massachusetts, 02214, United States

  • Mayo Clinic - Arizona

    RECRUITING

    Phoenix, Arizona, 85013, United States

  • Mayo Clinic - Florida

    RECRUITING

    Jacksonville, Florida, 32224, United States

    Contact Email: •••••@•••••

  • Mayo Clinic - Rochester

    RECRUITING

    Rochester, Minnesota, 55905, United States

    Contact Email: •••••@•••••

  • Mays Cancer Center

    NOT_YET_RECRUITING

    San Antonio, Texas, 78229, United States

  • Memorial Sloan Kettering Cancer Center

    RECRUITING

    New York, New York, 10065, United States

  • NYU Langone Health

    RECRUITING

    New York, New York, 10016, United States

  • Orlando Health Cancer Institute

    RECRUITING

    Orlando, Florida, 32806, United States

  • Peking Union Medical College Hospital

    RECRUITING

    Beijing, Beijing Municipality, 100730, China

  • Peter MacCallum Cancer Centre

    RECRUITING

    Melbourne, Victoria, Australia

  • Royal Brisbane and Women's Hospital

    RECRUITING

    Herston, Queensland, Australia

  • Royal North Shore Hospital

    RECRUITING

    Saint Leonards, New South Wales, Australia

  • Rutgers Cancer Institute

    RECRUITING

    New Brunswick, New Jersey, 08901, United States

  • Sanbo Brain Hospital, Capital Medical University

    RECRUITING

    Beijing, Beijing Municipality, 100093, China

  • Sir Charles Gairdner Hospital

    NOT_YET_RECRUITING

    Nedlands, Western Australia, 6009, Australia

  • St Vincents Hospital Sydney (Kinghorn)

    RECRUITING

    Darlinghurst, New South Wales, Australia

  • St. Joseph's Hospital and Medical Center

    RECRUITING

    Phoenix, Arizona, 85013, United States

  • Stanford University

    RECRUITING

    Palo Alto, California, 94304, United States

  • Sun Yat-sen University Cancer Center

    RECRUITING

    Guangzhou, Guangdong, 510060, China

  • The Alfred

    RECRUITING

    Melbourne, Victoria, Australia

  • The First Affiliated Hospital of Fujian Medical University

    RECRUITING

    Fuzhou, Fujian, 350005, China

  • Thomas Jefferson University Hospital

    RECRUITING

    Philadelphia, Pennsylvania, 19107, United States

    Contact Email: •••••@•••••

  • UPMC Hillman Cancer Center

    RECRUITING

    Pittsburgh, Pennsylvania, 15232, United States

  • UVA Health, Emily Couric Clinical Cancer Cente

    RECRUITING

    Charlottesville, Virginia, 22903, United States

  • University of Alabama

    RECRUITING

    Birmingham, Alabama, 35294, United States

  • University of California

    RECRUITING

    San Francisco, California, 94143, United States

  • University of California San Diego

    NOT_YET_RECRUITING

    La Jolla, California, 92093, United States

  • University of California, Los Angeles

    RECRUITING

    Los Angeles, California, 90095, United States

  • University of Chicago

    NOT_YET_RECRUITING

    Chicago, Illinois, 60637, United States

    Contact Email: •••••@•••••

  • University of Colorado Health Cancer Care

    RECRUITING

    Aurora, Colorado, 80045, United States

  • University of Florida Health

    RECRUITING

    Gainesville, Florida, 32608, United States

  • University of Kansas Medical Center

    RECRUITING

    Kansas City, Kansas, 66160, United States

  • University of Miami Health

    RECRUITING

    Miami, Florida, 33136, United States

  • University of Rochester Medical Center

    RECRUITING

    Rochester, New York, 14642, United States

  • University of Texas Southwestern Medical Center

    RECRUITING

    Dallas, Texas, 75390, United States

  • University of Wisconsin Health

    RECRUITING

    Madison, Wisconsin, 53792, United States

  • Vanderbilt-Ingram Cancer Center

    NOT_YET_RECRUITING

    Nashville, Tennessee, 37203, United States

  • Washington University

    RECRUITING

    St Louis, Missouri, 63110, United States

  • West China Hospital of Sichuan University

    RECRUITING

    Chengdu, Sichuan, 610041, China

  • Xiangya Hospital of Central South University

    RECRUITING

    Changsha, Hunan, 410008, China

  • Xuanwu Hospital, Capital Medical University

    RECRUITING

    Beijing, Beijing Municipality, 10053, China

  • Yale University

    RECRUITING

    New Haven, Connecticut, 06510, United States

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Other studies related to the condition(s) this trial covers.