Experimental drug rigosertib tested against aggressive skin cancer in rare disease patients

NCT ID NCT03786237

First seen Jun 25, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This small early-phase trial tested an experimental drug called rigosertib in just 2 people with a rare blistering skin disease (recessive dystrophic epidermolysis bullosa) who also had advanced skin cancer. The goal was to see if the drug could shrink tumors and whether it was safe. Rigosertib was given as oral capsules or intravenous infusions. Because only 2 patients took part, the results are very limited and cannot be generalized.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance
rigosertib (oral capsules or intravenous infusion)
What this could lead to
If it works, this could point toward a treatment for advanced skin cancer in people with recessive dystrophic epidermolysis bullosa.
What could go wrong
This is a very small, early-phase trial with only 2 patients, so results may not apply to others. The drug may not shrink tumors or could cause side effects.

This is an AI summary of the original study and may miss details. Read our disclaimer.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for EPIDERMOLYSIS BULLOSA DYSTROPHICA are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Conditions

The condition(s) this trial relates to.

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • EB House Austria/Dept. of Dermatology University Hospital

    Salzburg, State of Salzburg, 5020, Austria

More trials for these conditions

Other studies related to the condition(s) this trial covers.