New drug ravulizumab aims to control rare blood disorder aHUS

NCT ID NCT07308574

First seen Jun 26, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This study is testing the drug ravulizumab in 20 people with atypical hemolytic uremic syndrome (aHUS), a rare condition that causes blood clots and kidney damage. The goal is to see if the drug improves platelet counts and kidney function over 26 weeks. All participants receive the drug, and researchers will monitor safety and effectiveness.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

ravulizumab

What this could lead to

If successful, this study could confirm ravulizumab as a reliable treatment to control aHUS and prevent kidney damage.

What could go wrong

This is a small, single-arm study with no placebo group, so results may not be definitive. Ravulizumab also carries risks like increased susceptibility to infections.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

atypical hemolytic-uremic syndrome

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Research Site

    NOT_YET_RECRUITING

    Bunkyō City, 113-8655, Japan

  • Research Site

    NOT_YET_RECRUITING

    Hirakata-shi, 573-1191, Japan

  • Research Site

    RECRUITING

    Iruma-Gun, 350-0495, Japan

  • Research Site

    NOT_YET_RECRUITING

    Kyoto, 602-8566, Japan

  • Research Site

    NOT_YET_RECRUITING

    Matsumoto-shi, 390-8621, Japan

  • Research Site

    NOT_YET_RECRUITING

    Miyazaki, 889-1692, Japan

  • Research Site

    RECRUITING

    Nagoya, 466-8650, Japan

  • Research Site

    NOT_YET_RECRUITING

    Nara, 630-8581, Japan

  • Research Site

    NOT_YET_RECRUITING

    Nerima-ku, 177-8521, Japan

  • Research Site

    NOT_YET_RECRUITING

    Sapporo, 060-8638, Japan

  • Research Site

    NOT_YET_RECRUITING

    Shinjuku-ku, 162-8666, Japan

  • Research Site

    RECRUITING

    Tsu, 514-8507, Japan