Promising aHUS drug trial stalls after only 6 patients enrolled

NCT ID NCT03205995

First seen Jun 25, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This study tested a drug called narsoplimab (OMS721) for atypical hemolytic uremic syndrome (aHUS), a rare condition that causes blood clots and organ damage. The trial aimed to see if the drug could improve platelet counts and was safe for adults and adolescents. However, the study was terminated early and only enrolled 6 people, so we have very little information about how well it works.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

narsoplimab (a monoclonal antibody given by IV and daily injections)

What this could lead to

If successful, narsoplimab could offer a new treatment option for people with aHUS, potentially improving platelet counts and controlling the disease.

What could go wrong

The trial was terminated early with only 6 participants, so results are very limited. It is unclear if narsoplimab is safe or effective, and aHUS is a rare, serious condition.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

atypical hemolytic-uremic syndrome thrombotic microangiopathy

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Omeros Investigational Site

    Chicago, Illinois, 60643, United States

  • Omeros Investigational Site

    Vilnius, Lithuania

  • Omeros Investigational Site

    Lodz, Poland

  • Omeros Investigational Site

    New Taipei City, Taiwan