New hope for rare kidney disease: iptacopan shows promise in Long-Term trial

NCT ID NCT05795140

First seen May 13, 2026 · Last updated May 15, 2026 · Updated 1 time

Summary

This study looks at the long-term safety and effectiveness of the drug iptacopan in people with atypical hemolytic uremic syndrome (aHUS), a rare and serious kidney condition. About 65 adults who already completed a previous iptacopan study and are benefiting from the drug will continue taking it. Researchers will monitor side effects and check if the drug keeps the disease under control over time.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-••••

Locations

  • Novartis Investigative Site

    ACTIVE_NOT_RECRUITING

    São Paulo, São Paulo, 05403 000, Brazil

  • Novartis Investigative Site

    RECRUITING

    Rio de Janeiro, 22270-060, Brazil

  • Novartis Investigative Site

    RECRUITING

    Beijing, 100034, China

  • Novartis Investigative Site

    RECRUITING

    Ostrava, Poruba, 708 52, Czechia

  • Novartis Investigative Site

    ACTIVE_NOT_RECRUITING

    Nagpur, Maharashtra, 440015, India

  • Novartis Investigative Site

    RECRUITING

    Pune, Maharashtra, 411011, India

  • Novartis Investigative Site

    RECRUITING

    Iruma-gun, Saitama, 3500495, Japan

  • Novartis Investigative Site

    RECRUITING

    Mersin, Yenisehir, 33110, Turkey (Türkiye)

Conditions

Explore the condition pages connected to this study.