HHT nosebleed drug shows promise in long-term follow-up study

NCT ID NCT07018401

First seen Jun 26, 2026 · Last updated Jun 26, 2026 · Updated 1 time

Summary

This study follows 62 adults with hereditary hemorrhagic telangiectasia (HHT) who previously took pomalidomide in a clinical trial. Researchers want to see if the drug safely reduces nosebleed severity and the need for iron or blood transfusions over time. Participants take pomalidomide by mouth daily, and their bleeding scores, blood counts, and side effects are tracked.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

Pomalidomide (Pomalyst), a drug taken by mouth to reduce bleeding

What this could lead to

If it works, this could point toward a treatment that reduces severe nosebleeds and the need for iron infusions or blood transfusions in people with HHT.

What could go wrong

This is a small follow-up study with no placebo group, so results may be less reliable. Pomalidomide can cause side effects like low blood cell counts and blood clots.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

hereditary hemorrhagic telangiectasia

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Cleveland Clinic

    Cleveland, Ohio, 44195, United States

  • Johns Hopkins University

    Baltimore, Maryland, 21218, United States

  • Massachusetts General Hospital

    Boston, Massachusetts, 02114, United States

  • Mayo Clinic

    Rochester, Minnesota, 55905, United States

  • Medical College of Wisconsin

    Milwaukee, Wisconsin, 53226, United States

  • University of California-San Diego

    San Diego, California, 92093, United States

  • University of California-San Francisco

    San Francisco, California, 94143, United States

  • University of Florida

    Gainesville, Florida, 32610, United States

  • University of North Carolina, Chapel HIll

    Chapel Hill, North Carolina, 27599, United States

  • University of Pennsylvania

    Philadelphia, Pennsylvania, 19104, United States

  • University of Utah

    Salt Lake City, Utah, 84112, United States