MRNA therapy gives immune cells a temporary boost against rare infection disease

NCT ID NCT05189925

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This early-stage trial tests a new approach for chronic granulomatous disease (CGD), a genetic condition that leaves people vulnerable to severe infections. Researchers take a participant's own white blood cells, use mRNA to correct the genetic defect, and infuse the cells back. The goal is to see if the procedure is safe and feasible, and whether it can temporarily restore the cells' ability to kill germs. The study involves 25 adult males and includes a hospital stay for cell collection and infusion.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

mRNA-corrected white blood cells (gp91 Grans)

What this could lead to

If successful, this could provide a temporary way to restore infection-fighting ability in people with CGD, reducing infection risk.

What could go wrong

This is a very early Phase 1 trial with only 25 participants. The effect is temporary, and there may be side effects from the infusion or the cell collection process.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

chronic granulomatous disease granulomatous disease, chronic, X-linked Infections infectious disease Primary Immunodeficiency Diseases Toxemia

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • National Institutes of Health Clinical Center

    RECRUITING

    Bethesda, Maryland, 20892, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••