Lifesaving drug made available for rare fat disorder patients

NCT ID NCT02262832

First seen Jun 27, 2026 · Last updated Jul 17, 2026 · Updated 3 times

Summary

This study gives the drug metreleptin to people with generalized lipodystrophy, a rare condition that causes severe fat loss and leads to high blood fats and diabetes. Participants, aged 6 months and older, have already received metreleptin in past NIH studies but cannot get it in their home country. The goal is to keep their blood fats and blood sugar under control with ongoing treatment.

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Conditions

The condition(s) this trial relates to.

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • National Institutes of Health Clinical Center

    Bethesda, Maryland, 20892, United States

More trials for these conditions

Other studies related to the condition(s) this trial covers.