Gene therapy cocktail takes aim at Hard-to-Treat melanoma

NCT ID NCT01397708

First seen Jun 25, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This early-phase trial tested a new approach for people with advanced melanoma that cannot be removed by surgery. The treatment combines a gene therapy injected directly into tumors with an oral drug that activates the therapy. The goal was to see if the combination is safe and tolerable. 26 participants were enrolled, and the study is now complete.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

a gene therapy (Ad-RTS-hIL-12) injected into tumors plus an oral activator drug (veledimex)

What this could lead to

If it works, this could point toward a new way to treat advanced melanoma by boosting the immune system directly inside tumors.

What could go wrong

This is an early-phase trial with only 26 people, so results may not apply broadly. The treatment involves gene therapy and can cause side effects like inflammation.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

melanoma metastatic melanoma

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Atlantic Melanoma Center

    Morristown, New Jersey, 07960, United States

  • Fletcher Allen Health

    Burlington, Vermont, 05401, United States

  • Indiana University Health Goshen Center for Cancer Care

    Goshen, Indiana, 46526, United States

  • James Graham Brown Cancer Center

    Louisville, Kentucky, 40202, United States

  • Mary Crowley Cancer Research Center

    Dallas, Texas, 75201, United States

  • Oncology Specialists

    Park Ridge, Illinois, 60068, United States

  • St. Lukes

    Easton, Pennsylvania, 15232, United States

  • The Angeles Clinic

    Los Angeles, California, 90404, United States

  • Washington University

    St Louis, Missouri, 63110, United States