Hope for growth: new drug shows promise in Long-Term achondroplasia study
NCT ID NCT02724228
First seen Jun 27, 2026 · Last updated Jun 27, 2026
Summary
This study looks at the long-term safety and effects of a daily injection called BMN 111 in children with achondroplasia, a common form of dwarfism. It includes 30 children who have already taken the drug for two years in a previous study. The goal is to see if the drug remains safe and can help improve growth over time.
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This is a summary of
the original study
.
Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
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Locations
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Ann and Robert H. Lurie Childrens Hospital of Chicago
Chicago, Illinois, 60611, United States
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Baylor College of Medicine
Houston, Texas, 77030, United States
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Children's Hospital & Research Center Oakland
Oakland, California, 94609, United States
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Guys & St. Thomas NHS Foundation Trust Evelina Hospital
London, SE1 9RT, United Kingdom
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Harbor - UCLA Medical Center
Torrance, California, 90509, United States
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Institut Necker
Paris, 75015, France
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Johns Hopkins McKusick - Institute of Genetic Medicine
Baltimore, Maryland, 21287, United States
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Murdoch Children's Research Institute
Parkville, Victoria, 3052, Australia
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Vanderbilt University
Nashville, Tennessee, 37232-2578, United States