Could a daily pill boost growth in kids with hypochondroplasia?

NCT ID NCT06873035

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This study tests an oral drug called infigratinib in children with hypochondroplasia, a condition that causes short stature. The trial has two parts: first, all children receive the drug to see if it safely increases their growth rate; then, some will switch to a placebo to confirm the effect. Up to 24 children aged 3 to 11 will take part.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

infigratinib (oral drug)

What this could lead to

If successful, this could provide a treatment option to improve growth in children with hypochondroplasia.

What could go wrong

This is an early-to-mid-stage trial with only 24 participants. The drug may not work as hoped, and side effects could require dose changes or stopping treatment.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

bone disorder Dwarfism hereditary disease hypochondroplasia Mucopolysaccharidosis IV musculoskeletal system disorder osteochondrodysplasia

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Astrid Lindgren Children's Hospital

    Solna, Sweden, 17164, Sweden

  • Centre Hospitalier Universitaire (CHU) de Toulouse - Hôpital des Enfants

    Toulouse, France, 31059, France

  • Children's Hospital of Eastern Ontario Research Institute

    Ottawa, Ontario, K1H 8L1, Canada

  • Children's National Hospital

    Washington D.C., District of Columbia, 20010, United States

  • Childrens Hospital Colorado

    Aurora, Colorado, 80045, United States

  • Haukeland University Hospital

    Bergen, Norway, 5021, Norway

  • Hospital Pediátrico de Coimbra

    Coimbra, Portugal, 3000-602, Portugal

  • Hospital Vithas San Jose

    Vitoria-Gasteiz, Spain, 01008, Spain

  • Hôpital Femme Mère Enfant

    Bron, France, 69677, France

  • Hôpital Universitaire Necker-Enfants Malades

    Paris, France, 75015, France

  • Johns Hopkins School of Medicine

    Baltimore, Maryland, 21287, United States

  • KK Women's and Children's Hospital

    Singapore, Singapore, 229899, Singapore

  • London Health Services Center - Children's Hospital of Western Ontario

    London, Ontario, N6C 2R5, Canada

  • Manchester University

    Manchester, United Kingdom, M13 9WL, United Kingdom

  • Murdoch Children's Research Institute

    Parkville, Victoria, 3052, Australia

  • Paediatric Clinical Research Unit at Osla University Hospital

    Oslo, Norway, 0372, Norway

  • Sheffield Children's Hospital

    Sheffield, United Kingdom, S10 2TH, United Kingdom

  • UCSF Benioff Children's Hospital

    Oakland, California, 94609, United States

  • University of Missouri

    Columbia, Missouri, 65201, United States

  • University of Wisconsin Madison - Waisman Center Bone Dysplasia Clinic

    Madison, Wisconsin, 53705, United States

  • Université de Montréal - Centre Hospitalier Universitaire Sainte-Justine

    Montreal, Quebec, H3T 1C5, Canada

  • Vanderbilt University Medical Center

    Nashville, Tennessee, 37232, United States