New hope for babies with rare dwarfism: daily shot may boost growth

NCT ID NCT07126262

First seen Mar 28, 2026 · Last updated May 11, 2026 · Updated 4 times

Summary

This study tests a daily injection called vosoritide in 60 infants and toddlers (0 to 3 years old) with hypochondroplasia, a genetic condition that limits bone growth. The goal is to see if the drug safely improves height and growth rate compared to a placebo over 52 weeks. Participants must have a confirmed genetic diagnosis and meet height criteria.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Ann & Robert H. Lurie Children's Hospital of Chicago

    RECRUITING

    Chicago, Illinois, 60611, United States

  • Benioff Children's Hospital - Oakland

    RECRUITING

    Oakland, California, 94609, United States

  • Cedars-Sinai Medical Center

    NOT_YET_RECRUITING

    Los Angeles, California, 90048, United States

  • Children's Health Queensland Hospital and Health Service

    NOT_YET_RECRUITING

    South Brisbane, Queensland, 4101, Australia

  • Children's National Medical Center

    RECRUITING

    Washington D.C., District of Columbia, 20010, United States

  • Children's Wisconsin - Fox Valley Hospital

    NOT_YET_RECRUITING

    Neenah, Wisconsin, 54956, United States

  • Cook Children's Endocrinology

    NOT_YET_RECRUITING

    Fort Worth, Texas, 76104, United States

  • Fondazione Policlinico Universitario Agostino Gemelli IRCCS

    NOT_YET_RECRUITING

    Roma, Rome, 00168, Italy

  • Great Ormond Street Hospital

    NOT_YET_RECRUITING

    London, England, WC1N3BH, United Kingdom

  • Hospices Civils de Lyon - Hôpital Femme Mère Enfant

    NOT_YET_RECRUITING

    Bron, Rhone-Alps, 69500, France

  • Hôpital Bicêtre

    RECRUITING

    Le Kremlin-Bicêtre, Paris, 94270, France

  • IRCCS Istituto Giannina Gaslini

    RECRUITING

    Genova, 16147, Italy

  • Institute of Science Tokyo Hospital

    RECRUITING

    Tokyo, 113-8519, Japan

  • Kumamoto University Hospital

    RECRUITING

    Kumamoto, 860-8556, Japan

  • Myriad Trials

    NOT_YET_RECRUITING

    London, England, W1W 5DT, United Kingdom

  • Nihon University Itabashi Hospital

    RECRUITING

    Tokyo, 173-8610, Japan

  • Osaka Women's and Children's Hospital

    RECRUITING

    Osaka, 94-1101, Japan

  • Phoenix Children's Hospital - Thomas Campus (Main)

    RECRUITING

    Phoenix, Arizona, 85016, United States

  • Royal Children's Hospital Melbourne

    RECRUITING

    Parkville, Victoria, 3052, Australia

  • The Johns Hopkins University School of Medicine

    RECRUITING

    Baltimore, Maryland, 21205, United States

  • Tottori University Hospital

    RECRUITING

    Tottori, 683-0854, Japan

  • Uniklinik Köln

    RECRUITING

    Cologne, North Rhine-Westphalia, 50937, Germany

  • University of Minneasota Masonic Children's Hospital

    RECRUITING

    Minneapolis, Minnesota, 55454, United States

  • University of Missouri

    RECRUITING

    Columbia, Missouri, 65211, United States

  • Universitätskinderklinik Magdeburg

    NOT_YET_RECRUITING

    Magdeburg, Saxony-Anhalt, 39120, Germany

  • Universitätsklinikum des Saarlandes

    RECRUITING

    Homburg, Saarland, 66421, Germany

Conditions

Explore the condition pages connected to this study.