New anemia drug for MDS and myeloma patients shows early promise but trial halted

NCT ID NCT04582539

First seen Jun 25, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This study tested a daily pill called INCB000928 for people with anemia caused by myelodysplastic syndromes (MDS) or multiple myeloma. The goal was to see if it was safe and could raise red blood cell levels, reducing the need for transfusions. The trial was terminated early after enrolling only 22 participants, so we have limited information on how well it works.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

INCB000928

What this could lead to

If successful, this drug could help reduce or eliminate the need for blood transfusions in people with anemia from MDS or multiple myeloma.

What could go wrong

This was a very early (Phase 1/2) trial that was terminated before completion, so we have little data on safety or effectiveness. The drug may not work or could have side effects.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

anemia myelodysplastic syndrome Myelodysplastic Syndromes plasma cell myeloma

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Azienda Ospedaliero-Universitaria Careggi (Aouc)

    Florence, 50134, Italy

  • Barbara Ann Karmanos Cancer Hospital

    Detroit, Michigan, 48201, United States

  • Centre Hospitalier Universitaire de Nantes (Chu de Nantes) - Hotel-Dieu

    Nantes, 44093, France

  • Comitato Di Bioetica Della Fondazione Irccs Policlinico San Matteo

    Pavia, 27100, Italy

  • Florida Cancer Specialists

    Sarasota, Florida, 34232, United States

  • Hospices Civils de Lyon Centre Hospitalier Lyon Sud

    Pierre-Bénite, 69310, France

  • Institut Gustave Roussy

    Villejuif, 94800, France

  • Irccs Istituto Clinico Humanitas

    Rozzano, 20089, Italy

  • L Azienda Ospedaliero-Universitaria Di Bologna Policlinico S. Orsola - Malpighi

    Bologna, 40138, Italy

  • Md Anderson Cancer Center

    Houston, Texas, 77030, United States

  • Stanford Cancer Center

    Palo Alto, California, 94304, United States

  • Tulane Comprehensive Cancer Center

    New Orleans, Louisiana, 70112, United States

  • University of Cincinnati

    Cincinnati, Ohio, 45219, United States

  • University of Miami

    Miami, Florida, 33136, United States

  • Vanderbilt University Medical Center

    Nashville, Tennessee, 37232, United States