Gene therapy aims to restore hearing in children born deaf

NCT ID NCT05821959

First seen Nov 01, 2025 · Last updated May 15, 2026 · Updated 35 times

Summary

This trial tests a one-time gene therapy for people with profound hearing loss caused by otoferlin gene mutations. A harmless virus delivers a working copy of the gene into the inner ear during surgery. The study includes 22 participants of any age and focuses on safety and whether hearing improves.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Boston Children's Hospital

    RECRUITING

    Boston, Massachusetts, 02115, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Children's Hospital of Philadelphia

    RECRUITING

    Philadelphia, Pennsylvania, 19146, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Cincinnati Children's Hospital Medical Center

    RECRUITING

    Cincinnati, Ohio, 45229, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • National Taiwan University Hospital

    RECRUITING

    Taipei, 100, Taiwan

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • The Hospital for Sick Children [email protected] +1 (416) 813 6683

    RECRUITING

    Toronto, Ontario, M5G 1X8, Canada

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • University College London

    RECRUITING

    London, United Kingdom, NW1 2PG, United Kingdom

    Contact Email: •••••@•••••

  • University of California, San Francisco Benioff Children's Hospital

    RECRUITING

    San Francisco, California, 94158, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • University of Iowa

    RECRUITING

    Iowa City, Iowa, 52242, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Vanderbilt Bill Wilkerson Center

    RECRUITING

    Nashville, Tennessee, 37232, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.