Drug everolimus shows promise in slowing Children's brain tumors

NCT ID NCT01734512

First seen Jun 25, 2026 · Last updated Jun 26, 2026 · Updated 1 time

Summary

This study tested the drug everolimus in 65 children whose low-grade gliomas had come back or worsened. The goal was to see if the drug could stop or slow tumor growth. Children took everolimus pills daily, and doctors tracked tumor changes with MRI scans. The study focused on how many children remained progression-free after 6 months.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

Everolimus (a drug that blocks a protein called mTOR to slow tumor growth)

What this could lead to

If successful, everolimus could offer a new treatment option to control tumor growth and delay progression in children with low-grade gliomas.

What could go wrong

This is a small, single-arm phase 2 study without a placebo group, so results may not be definitive. The drug may cause side effects like mouth sores, infections, or metabolic changes.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

childhood low-grade glioma low-grade astrocytoma pilocytic astrocytoma

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Ann & Robert H. Lurie Children's Hospital of Chicago

    Chicago, Illinois, 60611, United States

  • Children's Hospital Los Angeles

    Los Angeles, California, 90027, United States

  • Children's Hospital Oakland

    Oakland, California, 94609, United States

  • Children's Hospitals and Clinics of Minneapolis

    Minneapolis, Minnesota, 55404, United States

  • Children's National Medical Center

    Washington D.C., District of Columbia, 20010, United States

  • Dana-Farber Cancer Institute

    Boston, Massachusetts, 02215, United States

  • Johns Hopkins University

    Baltimore, Maryland, 21218, United States

  • Nationwide Children's Hospital

    Columbus, Ohio, 43205, United States

  • Oregon Health & Science University

    Portland, Oregon, 97239, United States

  • St. Jude Children's Research Hospital

    Memphis, Tennessee, 38105, United States

  • St. Louis Children's Hospital, Washington University

    St Louis, Missouri, 63130, United States

  • The Children's Hospital Of Philadelphia

    Philadelphia, Pennsylvania, 19104, United States

  • University of California, Los Angeles

    Los Angeles, California, 90027, United States

  • University of California, San Diego Rady Children's Hospital

    San Diego, California, 92123, United States

  • University of California, San Francisco

    San Francisco, California, 94158, United States

  • University of Florida

    Gainesville, Florida, 32611, United States

  • University of Utah

    Salt Lake City, Utah, 84112, United States

  • University of Washington, Seattle

    Seattle, Washington, 98195, United States