New study monitors Eplontersen's effects during pregnancy and nursing

NCT ID NCT07205666

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This study follows up to 10 pregnant or breastfeeding individuals with transthyretin amyloidosis who have taken eplontersen, along with their infants. Researchers will track pregnancy complications, birth defects, and infant health during the first year of life. The goal is to describe safety outcomes, not to test the drug's effectiveness.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

eplontersen

What this could lead to

If successful, this study could provide important safety information for using eplontersen during pregnancy and breastfeeding.

What could go wrong

This is a very small study (10 participants) that only describes outcomes, not tests effectiveness. It may not detect rare risks or apply to all patients.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

familial amyloid neuropathy

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Research Site

    RECRUITING

    Frankfurt, Germany