Experimental drug targets rare blood condition in tiny pilot study

NCT ID NCT05102370

First seen Jun 27, 2026 ยท Last updated Jun 27, 2026

Summary

This early-phase study tested a drug called enasidenib in 4 people with a rare blood condition (CCUS) and a specific gene change (IDH2). The goal was to see if the drug could safely improve low blood cell counts. The study is complete, but results are not yet reported.

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As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Cleveland Clinic (Data Collection Only)

    Cleveland, Ohio, 44195, United States

  • Mayo Clinic (Data Collection Only)

    Rochester, Minnesota, 55905, United States

  • Memorial Sloan Kettering Bergen (Limited protocol activities)

    Montvale, New Jersey, 07645, United States

  • Memorial Sloan Kettering Cancer Center (All Protocol Activities)

    New York, New York, 10065, United States

  • Memorial Sloan Kettering Monmouth (All protocol activities)

    Middletown, New Jersey, 07748, United States

  • Memorial Sloan Kettering Nassau (Limited protocol activities)

    Rockville Centre, New York, 11553, United States

  • Memorial Sloan Kettering Suffolk-Commack (Limited protocol activities)

    Commack, New York, 11725, United States

  • Memorial Sloan Kettering Westchester (All Protocol Activities)

    Harrison, New York, 10604, United States

  • Memorial Sloan Kettering at Basking Ridge (All Protocol Activities)

    Basking Ridge, New Jersey, 07920, United States

  • Ohio State University (Data Collection Only)

    Columbus, Ohio, 43210, United States

  • Oregon Health & Science University (Data Collection Only)

    Portland, Oregon, 97239, United States

  • Washington University (Data Collection and Specimen Analysis)

    St Louis, Missouri, 63110, United States