New drug DYNE-101 aims to ease muscle stiffness in rare disease

NCT ID NCT05481879

First seen Nov 06, 2025 · Last updated May 08, 2026 · Updated 23 times

Summary

This study tests a new medicine called DYNE-101 for people with myotonic dystrophy type 1, a condition that causes muscle weakness and stiffness. The trial will check if the drug is safe and helps reduce muscle symptoms. About 116 adults will receive either DYNE-101 or a placebo through an IV, and the study lasts several years to see long-term effects.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • CHU de Nantes

    RECRUITING

    Nantes, 44093, France

    Contact Email: •••••@•••••

    Contact

  • Centro Clinico Nemo

    RECRUITING

    Milan, 20162, Italy

    Contact Email: •••••@•••••

    Contact

  • Charité - Universitätsmedizin Berlin

    RECRUITING

    Berlin, 10117, Germany

    Contact

    Contact Email: •••••@•••••

  • Fondazione Policlinico Universitario A Gemelli-Rome

    RECRUITING

    Rome, 00168, Italy

    Contact Email: •••••@•••••

    Contact

  • Indiana University School of Medicine

    RECRUITING

    Indianapolis, Indiana, 46202, United States

    Contact

    Contact Email: •••••@•••••

  • Institut de Myologie

    RECRUITING

    Paris, 75013, France

    Contact Email: •••••@•••••

    Contact

  • John Walton Muscular Dystrophy Research Centre

    RECRUITING

    Newcastle upon Tyne, United Kingdom

    Contact

    Contact Email: •••••@•••••

  • Ludwig Maximilians University, Munich - Friedrich Baur Institut

    RECRUITING

    Munich, 80336, Germany

    Contact

    Contact Email: •••••@•••••

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  • NZCR Auckland

    RECRUITING

    Auckland, 1023, New Zealand

    Contact

    Contact Email: •••••@•••••

  • Neurology Rare Disease Center

    RECRUITING

    Denton, Texas, 76208, United States

    Contact

    Contact Email: •••••@•••••

  • Radboud Medical Center

    RECRUITING

    Nijmegen, Netherlands

    Contact Email: •••••@•••••

    Contact

  • Salford Royal Hospital

    RECRUITING

    Salford, M6 8HD, United Kingdom

    Contact Email: •••••@•••••

    Contact

  • St. Vincent's Hospital

    RECRUITING

    Fitzroy, Victoria, 3065, Australia

    Contact Email: •••••@•••••

    Contact

  • University College London Hospitals

    RECRUITING

    London, NW1 2BU, United Kingdom

    Contact

    Contact Email: •••••@•••••

  • University of Iowa

    RECRUITING

    Iowa City, Iowa, 52242, United States

    Contact

    Contact Email: •••••@•••••

  • University of Rochester Medical Center

    RECRUITING

    Rochester, New York, 14642, United States

    Contact

    Contact Email: •••••@•••••

  • Virginia Commonwealth University (VCU)

    RECRUITING

    Richmond, Virginia, 23298, United States

    Contact Email: •••••@•••••

    Contact Email: •••••@•••••

    Contact

Conditions

Explore the condition pages connected to this study.