The Children's Hospital Of Zhejiang University School Of Medicine

This study tests whether adding the drug selinexor to standard chemotherapy can help children with a rare, high-risk form of acute myeloid leukemia (AML) caused by a NUP98 gene change. Ten children will receive the combination during their first two rounds of chemo. The goal is t…

This early-stage study tests a gene therapy called AAV9.hMCOLN1co in one child with Mucolipidosis Type IV, a rare genetic disorder. The goal is to see if the treatment is safe and can help control the disease. Participants must be between 1.5 and 8 years old and have a confirmed …

This early-stage study tests whether a special type of immune cell, called CAR-T, can safely treat people with severe lupus that hasn't improved with standard treatments. The therapy targets a protein called CD19 on immune cells to calm the overactive immune system. The main goal…

This study aims to create an intelligent ultrasound system that can automatically identify different types of neuroblastoma tumors in children and predict how aggressive they are. Researchers will use ultrasound images and medical records from 300 children to train the AI. The go…