Askbio Inc
Clinical trials sponsored by Askbio Inc, explained in plain language.
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Gene therapy breakthrough? new trial targets Parkinson's brain cells
Disease control Recruiting nowThis study tests a gene therapy called AAV2-GDNF for people with moderate Parkinson's disease. The treatment is delivered directly into the brain to help protect and repair cells that control movement. About 127 adults aged 45-75 will take part, and the study will compare the the…
Phase: PHASE2 • Sponsor: AskBio Inc • Aim: Disease control
Last updated May 15, 2026 11:57 UTC
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Gene therapy trial hopes to slow rare muscle disease
Disease control Recruiting nowThis study tests a single dose of a gene therapy called AB-1003 in 10 adults with a rare genetic muscle disease (LGMD2I/R9) that causes progressive weakness. The main goal is to check safety, not yet to prove it works. Participants must be able to walk 10 meters in under 30 secon…
Phase: PHASE1, PHASE2 • Sponsor: AskBio Inc • Aim: Disease control
Last updated May 13, 2026 16:03 UTC
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One-shot gene therapy aims to free pompe patients from lifelong infusions
Disease control Recruiting nowThis study tests a single intravenous dose of AB-1009 gene therapy in 12 adults with late-onset Pompe disease. Participants must have been on enzyme replacement therapy for at least 6 months. The goal is to see if the treatment is safe and can reduce or replace the need for regul…
Phase: PHASE1, PHASE2 • Sponsor: AskBio Inc • Aim: Disease control
Last updated May 11, 2026 20:52 UTC