Askbio Inc

This study follows people with Parkinson's disease or a related condition who previously received an experimental gene therapy called AB-1005. Researchers want to understand the long-term safety of the treatment and see how well its effects last over time. The study is observatio…

This is an early-stage safety study testing a new gene therapy called ACTUS-101 for adults with late-onset Pompe disease. The therapy aims to deliver a working copy of a missing gene to the liver to help the body produce a needed enzyme. The study will monitor seven participants …

This study is testing whether a single dose of an experimental gene therapy called AB-1002 can help adults with advanced heart failure. About 150 participants with a specific type of heart failure will receive either the therapy or a placebo, delivered directly into their heart's…

This study aims to better understand how early Parkinson's disease and a related condition called multiple system atrophy progress over time. Researchers will follow 150 participants for 18 months, tracking their symptoms, movement abilities, and quality of life. The goal is to g…