WILSON DISEASE
Clinical trials for WILSON DISEASE explained in plain language.
Never miss a new study
Get alerted when new WILSON DISEASE trials appear
Sign up with your email to follow new studies for WILSON DISEASE, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
By submitting, you agree to our Terms of use
-
Gene therapy breakthrough aims to control copper in wilson disease
Disease control OngoingThis study tests a new gene therapy called UX701 for adults with Wilson disease, a genetic condition that causes copper buildup. The goal is to see if a single dose can help the body control copper levels safely, possibly reducing the need for daily medications. About 82 particip…
Matched conditions: WILSON DISEASE
Phase: PHASE1, PHASE2 • Sponsor: Ultragenyx Pharmaceutical Inc • Aim: Disease control
Last updated May 17, 2026 03:54 UTC
-
New study aims to pave way for better wilson disease trials
Knowledge-focused OngoingThis study looks at how people with Wilson Disease manage their condition and what influences their decision to join clinical research. About 30 adults with confirmed Wilson Disease will complete surveys and provide blood samples. The goal is to gather information that will help …
Matched conditions: WILSON DISEASE
Sponsor: Prime Medicine, Inc. • Aim: Knowledge-focused
Last updated May 15, 2026 11:54 UTC
-
Gene therapy for wilson disease: a closer look with PET scans
Knowledge-focused ENROLLING_BY_INVITATIONThis study uses special PET scans to see how gene therapy (UX704) changes copper levels in the liver and body of people with Wilson disease. Only 5 patients who already received the gene therapy will join. The goal is to understand if the therapy helps the liver handle copper bet…
Matched conditions: WILSON DISEASE
Sponsor: Thomas Damgaard Sandahl • Aim: Knowledge-focused
Last updated May 11, 2026 20:53 UTC