Tiny trial uses PET scans to peek at gene therapy for wilson disease

NCT ID NCT07159581

First seen Jun 26, 2026 · Last updated Jun 26, 2026

Summary

This study will use special PET scans to see how gene therapy (UX704) changes copper distribution in the bodies of 5 people with Wilson disease. The goal is to understand if the therapy helps the liver handle copper better. It is an early, observational imaging study, not a test of whether the therapy cures the disease.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

UX704 gene therapy

What this could lead to

If successful, this could show that gene therapy helps Wilson disease patients process copper better, pointing toward a more effective treatment.

What could go wrong

This is a very small study (5 people) that only looks at imaging results, not long-term health outcomes. It may not prove the therapy works or is safe.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

Wilson disease

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Aarhus University Hospital

    Aarhus, Aarhus N, 8200, Denmark