Wilson disease patients sought for survey to shape gene editing research
NCT ID NCT07226622
First seen Jun 24, 2026 · Last updated Jun 27, 2026 · Updated 1 time
Summary
This study surveys 30 adults with Wilson disease to learn about their daily management, treatment adherence, and interest in gene editing clinical trials. By gathering this information, researchers hope to design better future studies for potential gene therapies targeting specific ATP7B mutations.
What this could mean
Our plain-language read of the trial. This is informational only — not medical advice or a prediction.
What this could lead to
If successful, this study could help design better future clinical trials for gene editing treatments in Wilson disease.
What could go wrong
This is a small, observational prescreening study with only 30 participants, so it won't directly test any treatment or provide health benefits.
Disclaimer
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This is a summary of
the original study
.
Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
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Locations
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American Research Corporation
San Antonio, Texas, 78215, United States
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Massachusetts General Hospital
Boston, Massachusetts, 02114, United States
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Northwestern University
Chicago, Illinois, 60611, United States
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University of California Davis Health
Sacramento, California, 95817, United States
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University of California Los Angeles Medical Center
Los Angeles, California, 90027, United States
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University of Michigan Medicine
Ann Arbor, Michigan, 48109, United States
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Yale New Haven Hospital
New Haven, Connecticut, 06520, United States