Prime Medicine, Inc.
Clinical trials sponsored by Prime Medicine, Inc., explained in plain language.
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Groundbreaking gene therapy aims to fix immune system in rare disease
Disease control ENROLLING_BY_INVITATIONThis early-stage trial tests a new gene therapy (PM359) for people with a rare immune disorder called chronic granulomatous disease (CGD). The treatment takes a patient's own blood stem cells, fixes a specific genetic error using a precise editing tool called prime editing, and r…
Phase: PHASE1, PHASE2 • Sponsor: Prime Medicine, Inc. • Aim: Disease control
Last updated Jun 27, 2026 12:04 UTC
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Wilson disease patients sought for survey to shape gene editing research
Knowledge-focused OngoingThis study surveys 30 adults with Wilson disease to learn about their daily management, treatment adherence, and interest in gene editing clinical trials. By gathering this information, researchers hope to design better future studies for potential gene therapies targeting specif…
Sponsor: Prime Medicine, Inc. • Aim: Knowledge-focused
Last updated Jun 27, 2026 12:31 UTC