Can a single infusion rewrite the genetic code behind wilson disease?
⭐️ CURE ⭐️
Not yet recruiting
This trial tests an experimental therapy called PM577a, which uses prime editing to correct a common genetic mutation that causes Wilson disease. The treatment is given as a single intravenous infusion and aims to restore the liver's ability to remove excess copper. The study inc…
Phase: PHASE1, PHASE2 • Sponsor: Prime Medicine, Inc. • Aim: ⭐️ CURE ⭐️
Last updated Aug 13, 2026 00:00 UTC