LEBER HEREDITARY OPTIC NEUROPATHY
Clinical trials for LEBER HEREDITARY OPTIC NEUROPATHY explained in plain language.
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Gene therapy aims to halt blindness from rare eye disease
Disease control CompletedThis study tested a gene therapy called GS010 in 98 people with Leber hereditary optic neuropathy (LHON), a genetic condition that causes sudden vision loss. Participants received injections into both eyes and were followed for up to 5 years. The goal was to see if the treatment …
Matched conditions: LEBER HEREDITARY OPTIC NEUROPATHY
Phase: PHASE3 • Sponsor: GenSight Biologics • Aim: Disease control
Last updated May 17, 2026 06:19 UTC
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Gene therapy injection shows promise for inherited blindness
Disease control CompletedThis study tested a gene therapy called GS010 in 19 adults with Leber Hereditary Optic Neuropathy (LHON), a rare inherited condition that causes sudden vision loss. Participants received a single injection of the therapy into one eye to see if it was safe and tolerable. The main …
Matched conditions: LEBER HEREDITARY OPTIC NEUROPATHY
Phase: PHASE1, PHASE2 • Sponsor: GenSight Biologics • Aim: Disease control
Last updated May 17, 2026 06:19 UTC
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Gene therapy for rare blindness shows promise in Long-Term study
Disease control CompletedThis study followed 62 people with Leber Hereditary Optic Neuropathy (LHON) who received GS010 gene therapy in earlier trials. Researchers tracked eye safety and vision changes for up to 5 years after treatment. The goal was to see if the therapy remains safe and helps maintain o…
Matched conditions: LEBER HEREDITARY OPTIC NEUROPATHY
Phase: PHASE3 • Sponsor: GenSight Biologics • Aim: Disease control
Last updated May 12, 2026 13:41 UTC
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Researchers track vision loss and life impact in rare eye disease
Knowledge-focused CompletedThis study looked at 44 people with a confirmed genetic diagnosis of Leber Hereditary Optic Neuropathy (LHON), a rare inherited eye disease that causes vision loss. Researchers reviewed medical records and asked participants about their vision, quality of life, and the financial …
Matched conditions: LEBER HEREDITARY OPTIC NEUROPATHY
Sponsor: GenSight Biologics • Aim: Knowledge-focused
Last updated May 14, 2026 12:06 UTC