FRAGILE X SYNDROME
Clinical trials for FRAGILE X SYNDROME explained in plain language.
Never miss a new study
Get alerted when new FRAGILE X SYNDROME trials appear
Sign up with your email to follow new studies for FRAGILE X SYNDROME, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
By submitting, you agree to our Terms of use
-
CBD gel tested for Long-Term safety in fragile x kids and young adults
Disease control OngoingThis study looks at the long-term safety of a CBD gel (ZYN002) applied to the skin for children, teens, and young adults with Fragile X syndrome. Participants from two earlier studies will use the gel twice daily for 52 weeks. The main goal is to check for side effects, with a se…
Matched conditions: FRAGILE X SYNDROME
Phase: PHASE2, PHASE3 • Sponsor: Zynerba Pharmaceuticals, Inc. • Aim: Disease control
Last updated Jun 27, 2026 12:38 UTC
-
New drug shows promise for Long-Term fragile x management
Disease control OngoingThis 4-year study tests the long-term safety of the drug BPN14770 (zatolmilast) in 314 people with Fragile X syndrome who completed earlier trials. Participants include adult males and adolescents. The main goal is to see if the drug is safe over time, with secondary measures loo…
Matched conditions: FRAGILE X SYNDROME
Phase: PHASE3 • Sponsor: Tetra Discovery Partners • Aim: Disease control
Last updated Jun 27, 2026 07:53 UTC
-
Newborn screening study aims to catch rare diseases at birth
Diagnosis OngoingThis study offers voluntary screening for newborns in North Carolina to detect a wide range of rare health conditions early. Using a small blood sample already collected at birth, the program tests for dozens of disorders, including spinal muscular atrophy, cystic fibrosis, and m…
Matched conditions: FRAGILE X SYNDROME
Sponsor: RTI International • Aim: Diagnosis
Last updated Jul 02, 2026 02:00 UTC
-
Can a single dose ease fragile x? new trial tests three drugs
Symptom relief OngoingThis study tests whether a single dose of baclofen, roflumilast, or memantine can improve brain activity and symptoms in adults with Fragile X syndrome. Forty-five participants aged 18 to 45 will receive each drug or a placebo in separate sessions. The main goal is to measure cha…
Matched conditions: FRAGILE X SYNDROME
Phase: PHASE2 • Sponsor: Children's Hospital Medical Center, Cincinnati • Aim: Symptom relief
Last updated Jun 27, 2026 08:06 UTC
-
Can a simple test track ADHD med effects in kids with intellectual disability?
Symptom relief ENROLLING_BY_INVITATIONThis study looks at whether a set of thinking and memory tests can detect changes caused by a stimulant medication in children aged 6 to 17 who have both intellectual disability and ADHD. About 68 participants will receive either the medication or a placebo, then switch after a b…
Matched conditions: FRAGILE X SYNDROME
Phase: PHASE1 • Sponsor: University of California, Davis • Aim: Symptom relief
Last updated Jun 27, 2026 08:04 UTC