BATTEN DISEASE
Clinical trials for BATTEN DISEASE explained in plain language.
Never miss a new study
Get alerted when new BATTEN DISEASE trials appear
Sign up with your email to follow new studies for BATTEN DISEASE, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
By submitting, you agree to our Terms of use
-
Tracking a hopeful gene therapy for a devastating childhood disease
Disease control OngoingThis study is tracking 10 children with CLN6 Batten disease for up to 5 years after they received a single, experimental gene therapy. The goal is to understand the long-term safety and whether the treatment continues to help slow the progression of this fatal neurological disord…
Matched conditions: BATTEN DISEASE
Sponsor: Emily de los Reyes • Aim: Disease control
Last updated Mar 30, 2026 14:33 UTC
-
Study seeks to measure how treatment affects development in devastating childhood disease
Knowledge-focused ENROLLING_BY_INVITATIONThis study aims to understand how a rare, fatal childhood brain disease called CLN2 Batten disease affects children's development. Researchers will track 30 children, comparing those receiving a treatment called cerliponase alfa to those who are untreated. The goal is to measure …
Matched conditions: BATTEN DISEASE
Sponsor: Jessica Scherr • Aim: Knowledge-focused
Last updated Apr 02, 2026 00:41 UTC