BATTEN DISEASE

Clinical trials for BATTEN DISEASE explained in plain language.

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Trials to join now! 4 Not yet recruiting 1 Not yet finished but already full! 2 Completed 1

Experimental drug shows promise for rare batten disease

Disease control Completed

This study tested the safety and effectiveness of the drug miglustat in 6 adults aged 17 and older with CLN3 Batten disease, a rare genetic disorder that damages the nervous system. Participants took miglustat for up to 104 weeks to see how the body processes the drug and whether…

Matched conditions: BATTEN DISEASE

Phase: PHASE1, PHASE2 • Sponsor: Beyond Batten Disease Foundation • Aim: Disease control

Last updated May 15, 2026 11:56 UTC

BATTEN DISEASE

Get alerted when new BATTEN DISEASE trials appear

Experimental drug shows promise for rare batten disease