BATTEN DISEASE

Clinical trials for BATTEN DISEASE explained in plain language.

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Trials to join now! 5 Not yet recruiting 1 Not yet finished but already full! 3 Completed 1

Experimental drug miglustat tested for rare batten disease

Disease control Completed

This study tested the drug miglustat in 6 adults aged 17 and older with CLN3 Batten disease, a rare genetic disorder that causes nerve damage. The goal was to see if the drug is safe and to find the best dose over 2 years. Researchers tracked side effects and how the drug moved t…

Matched conditions: BATTEN DISEASE

Phase: PHASE1, PHASE2 • Sponsor: Beyond Batten Disease Foundation • Aim: Disease control

Last updated Jun 26, 2026 14:56 UTC

BATTEN DISEASE

Get alerted when new BATTEN DISEASE trials appear

Experimental drug miglustat tested for rare batten disease