New study aims to measure how CLN2 disease affects Children's development

NCT ID NCT03862274

ENROLLING_BY_INVITATION Knowledge-focused Sponsor: Jessica Scherr Source: ClinicalTrials.gov โ†—

First seen Jun 27, 2026 ยท Last updated Jun 27, 2026

Summary

This study looks at how children with CLN2 Batten disease develop over time, including their thinking, language, and motor skills. Researchers will compare children who receive treatment (cerliponase alfa) with those who do not. The goal is to find better ways to measure the disease's impact and improve care. About 30 children will take part.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary โ€” we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

neuronal ceroid lipofuscinosis neuronal ceroid lipofuscinosis 2 neuronal ceroid lipofuscinosis 3 Neuronal Ceroid-Lipofuscinoses

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Nationwide Children's Hospital

    Columbus, Ohio, 43205, United States