New study aims to measure how CLN2 disease affects Children's development
NCT ID NCT03862274
First seen Jun 27, 2026 · Last updated Jun 27, 2026
Summary
This study looks at how children with CLN2 Batten disease develop over time, including their thinking, language, and motor skills. Researchers will compare children who receive treatment (cerliponase alfa) with those who do not. The goal is to find better ways to measure the disease's impact and improve care. About 30 children will take part.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
Locations
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Nationwide Children's Hospital
Columbus, Ohio, 43205, United States
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