BATTEN DISEASE
Clinical trials for BATTEN DISEASE explained in plain language.
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New cell booster may help cord blood transplants reach the brain in kids with rare diseases
Disease control Recruiting nowThis early-stage study tests whether adding special cells (DUOC-01) to a standard cord blood transplant is safe for children with inherited metabolic diseases that damage the brain. About 40 participants, from 1 week to 21 years old, will receive the cells via a spinal injection.…
Matched conditions: BATTEN DISEASE
Phase: PHASE1 • Sponsor: Joanne Kurtzberg, MD • Aim: Disease control
Last updated May 17, 2026 03:28 UTC
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Scientists seek clues to deadly batten disease in new study
Knowledge-focused Recruiting nowThis study aims to learn more about Batten disease (CLN3), a rare and deadly genetic disorder that affects the brain and nervous system. Researchers will collect samples like blood, spinal fluid, and skin from up to 300 people with CLN3 and their family members. The goal is to fi…
Matched conditions: BATTEN DISEASE
Sponsor: Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) • Aim: Knowledge-focused
Last updated May 17, 2026 03:30 UTC
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Major study tracks rare brain disorders to unlock disease secrets
Knowledge-focused Recruiting nowThis study follows 1,500 people with rare genetic brain diseases to learn how these conditions progress. Researchers will track thinking, movement, and daily living skills over time. The goal is to better understand the diseases and how treatments might affect them.
Matched conditions: BATTEN DISEASE
Sponsor: University of Pittsburgh • Aim: Knowledge-focused
Last updated May 13, 2026 16:00 UTC
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Scientists track batten disease to unlock clues for future treatments
Knowledge-focused Recruiting nowThis study follows 500 children and adults with Batten disease to learn how the condition changes over time. Researchers will measure movement, thinking, behavior, and daily function using special tests. The goal is to better understand the disease and improve tools for future cl…
Matched conditions: BATTEN DISEASE
Sponsor: University of Rochester • Aim: Knowledge-focused
Last updated May 12, 2026 13:42 UTC