Scientists track batten disease to unlock its secrets
NCT ID NCT01873924
First seen Jun 26, 2026 · Last updated Jun 26, 2026
Summary
This study follows 500 children and adults with Batten disease to learn how the condition naturally changes over time. Researchers will measure movement, thinking, behavior, and daily function using a special rating scale. The goal is to better understand the disease and improve future clinical trials.
What this could mean
Our plain-language read of the trial. This is informational only — not medical advice or a prediction.
- What this could lead to
- If successful, this study could provide a clearer picture of how Batten disease progresses, which may help design future treatments and improve clinical care.
- What could go wrong
- This is an observational study, not a treatment trial. It will not directly benefit participants, and results may take years to influence care.
This is an AI summary of the original study and may miss details. Read our disclaimer.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
Locations
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University of Rochester
RECRUITINGRochester, New York, 14642, United States
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