New transplant trial aims to reset immune system in rare genetic disorder
NCT ID NCT01861106
Summary
This study is testing whether a stem cell transplant from a donor can treat GATA2 deficiency, a genetic condition that causes serious infections and blood cancers. Participants (ages 6-70) will receive chemotherapy and then donor stem cells to try to rebuild their immune system. The goal is to see if the transplant can restore healthy blood cell production and reverse the disease's effects.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
Get updates
Get notified about this study
Sign up to get updates when this study changes or when new studies for MDS are added.
Genom att skicka in godkänner du våra Användarvillkor
Contacts and locations
Show contact details
Enter your email to view the contact information for this study.
Genom att skicka in godkänner du våra Användarvillkor
Study contacts
-
Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
-
National Institutes of Health Clinical Center
RECRUITINGBethesda, Maryland, 20892, United States
Conditions
Explore the condition pages connected to this study.