Hope for Friedreich's ataxia: new drug trial seeks Long-Term answers
NCT ID NCT06447025
First seen Apr 04, 2026 · Last updated May 23, 2026 · Updated 11 times
Summary
This study is testing the long-term safety and effects of an experimental drug called CTI-1601 in people with Friedreich's ataxia, a rare genetic disease that affects movement and heart function. It includes about 85 participants aged 2 and older, some of whom have taken the drug before and some who haven't. Researchers will monitor side effects, heart health, motor skills, and daily living abilities over time.
Disclaimer
Read more
Show less
This is a summary of
the original study
.
Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
Get updates
Get notified about this study
Sign up to get updates when this study changes or when new studies for FRIEDREICH ATAXIA are added.
Genom att skicka in godkänner du våra Användarvillkor
Contacts and locations
Show contact details
Enter your email to view the contact information for this study.
Genom att skicka in godkänner du våra Användarvillkor
Study contacts
-
Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
-
Children's Hospital of the University of Pennsylvania (CHOP)
RECRUITINGPhiladelphia, Pennsylvania, 19104, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact Phone: •••-•••-•••• Email: •••••@•••••
-
Clinilabs Drug Development, Corp.
RECRUITINGEatontown, New Jersey, 07724, United States
-
Fixel Institute for Neurological Disease, University of Florida Health
ACTIVE_NOT_RECRUITINGGainesville, Florida, 32608, United States
-
Morsani Center for Advanced Health Care, University of South Florida Health
RECRUITINGTampa, Florida, 33612, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact Phone: •••-•••-•••• Email: •••••@•••••
-
Ohio State University United States
ACTIVE_NOT_RECRUITINGColumbus, Ohio, 43210, United States
-
Uncommon Cures
RECRUITINGChevy Chase, Maryland, 20815, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact Phone: •••-•••-•••• Email: •••••@•••••
-
University of California Los Angeles
RECRUITINGLos Angeles, California, 90095, United States
-
University of Iowa
RECRUITINGIowa City, Iowa, 52242, United States
Conditions
Explore the condition pages connected to this study.